恩西地平是可口服,可逆,选择性的 IDH2 突变酶抑制剂,抑制IDH2R140Q 和 IDH2R172K 的 IC50 分别为100 和 400 nM,是一种药物,用于治疗复发或难治性急性髓细胞白血病患者中的异柠檬酸脱氢酶2(IDH2)基因的特异性突变.
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